New biotech discoveries include CRISPR-induced conception and a biomarker for predicting breast cancer recurrences.
The protein Pax5, which organizes genetic information for cells, may also protect against cancer and other diseases, researchers found.
Scientists have demonstrated how mutations in cell proteins known as “splicing factors” can cause the eye disease retinitis pigmentosa.
Researchers accidentally reprogrammed mature neurons into dopamine-producing neurons—a discovery that could spark new therapies for brain diseases.
CRISPR-GO allows scientists to reorganize the genome—taking specific pieces and placing them at new locations in a cell’s nucleus.
Spark Therapeutics announced encouraging preclinical data on SPK-3006, its gene therapy to treat the muscle disorder Pompe.
Two separate teams used modified versions of CRISPR-Cas9 to correct rare but lethal inherited liver diseases.
Some microRNAs could serve as prognostic markers of Crohn's and open the possibility of developing personalized therapies.
A mouse study and a human population study find chemotherapy might compound cognitive deficits in cancer patients with the APOE4 gene.
An NCI team is reporting promising results from a small trial of a dendritic-cell vaccine in patients whose tumors overexpress HER2.