Duchenne muscular dystrophy

The Top Line
Podcast

What were the biggest clinical trial flops of 2024?

This week on "The Top Line," we dive into the biggest clinical trial failures of 2024 and discuss what the industry can learn from these setbacks.
rocket ship blast off fire away take off

Solid soars as early DMD gene therapy data beat expectations

Feb 18, 2025 8:10am
DNA gene therapy gene editing helix CRISPR

Regenxbio starts pivotal study for DMD gene therapy

Nov 18, 2024 2:24pm
Needle sewing thread and fabric

DMD gene therapy uses cells to stitch together mRNA in mice

Nov 14, 2024 3:10pm
Blue race track

Capricor shares more data for DMD therapy after initiating BLA

Oct 11, 2024 11:50am
Duchenne muscular dystrophy genetic test DMD

Young participant in Pfizer's DMD gene therapy trial dies

May 7, 2024 4:29pm