beta thalassemia

red blood cells

Biotech

Vertex and Orna team up to develop new blood disorder treatments

Vertex is hoping to build out its inherited blood disease portfolio, teaming up with Orna to develop next-gen gene therapies for SCD and TDT.

Gabrielle Masson Jan 7, 2025 7:00am

Image of a crossing guard sign in the foreground with a crossing guard directing traffic in the background

FDA advisers wave through first CRISPR-based therapy

Nov 1, 2023 11:07am

photo of a royal flush laid out on the poker table with chips scattered nearby

CRISPR on hunt for pipeline partners and enticing delivery tech

Oct 19, 2023 10:35am

sickle cell blood anemia

Pfizer drops sickle cell collab with Syros inherited from GBT

Jul 24, 2023 10:23am

Step closer race run

Vertex-CRISPR drug posts phase 3 wins, secures PDUFA date

Jun 9, 2023 7:30am

Ionis headquarters

Ionis' midphase misses send rare disease prospects to the abyss

May 4, 2023 10:25am