Keyword: Alnylam Pharmaceuticals
Pfizer’s ATTR drug tafamidis has hit the mark in a phase 3 trial, setting up regulatory filings and a challenge to rivals Alnylam and Ionis/Akcea.
Eidos' $106 million IPO comes on the heels of a $64 million series B and will support phase 2 and phase 3 trials of its TTR amyloidosis drug.
BOSTON—We caught up John Maraganore at this year's meeting to ask him about drug pricing, immigration and the culture at biotech versus pharma companies.
After a turbulent year, Prothena is reorganizing to rally its resources around what remains in its neuroscience pipeline.
Alnylam is gearing up to move RNAi therapies for central nervous system disorders into the clinic.
The initiative taps into the networks Invitae has built up to connect sponsors to patients and the clinicians responsible for their care.
Akcea suffered the setback after the FDA asked for more time to review its response to requests for information on the rare disease antisense drug.
Details on Westphal's new venture are sketchy, with a corporate filing saying the company is "developing immunotherapy treatments for cancer."
The success positions Alexion to file for approval and shield itself from an anticipated assault on its paroxysmal nocturnal hemoglobinuria franchise.
The new angle comes from an exploratory post hoc analysis which linked the RNAi therapy to a 50% drop in hospitalization and mortality over placebo.