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achondroplasia
Biotech
BioMarin's R&D head hopes pipeline of good ideas won't 'dry out'
Using a two-pronged strategy, BioMarin is doubling down on therapeutic areas it has scored in previously.
Darren Incorvaia
Feb 21, 2025 7:00am
Pfizer punts pair of orphan drugs amid rare disease R&D rethink
Jan 31, 2023 9:15am
BridgeBio’s QED Therapeutics picks up discarded Novartis cancer drug
Jan 30, 2018 11:16am