Gene editing pioneer Sangamo BioSciences has its sights set on curing hemophilia, a rare disorder in which the blood doesn't clot normally.

Duke University could be handed as much as $19 million from the National Institutes of Health to manage first-in-human studies for conditions such as Alzheimer…

Researchers at Northwestern University are revisiting the idea of gene therapy to treat depression.

Researchers at the Stanford University School of Medicine have shown that they can rapidly produce populations of at least 12 cell types, including bone, heart…

Researchers believe they may have found how Alzheimer’s disease spreads across one area of the brain at its early stages to across the whole organ--and that…

Scientists at the National Institutes of Health have singled out a molecule that could be useful to treat both a rare disorder--Gaucher disease--as well as the…

Researchers from the Hebrew University of Jerusalem have developed a new molecule that can protect the brain from inflammation and other effects following a…

Stanford scientists have partially restored vision to mice thought to have lost it permanently in an approach that could eventually lead to the restoration of…