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rare diseases
Biotech
As pharma eyes shiny obesity drugs, Vertex tops orphan drug list
Vertex’s cystic fibrosis triple combo is the top orphan pipeline drug, amid shifting sentiments in the pharma industry for rare disease drugs.
Annalee Armstrong
Apr 24, 2024 12:01am
J&J funds Rallybio in risk-busting rare pregnancy disease pact
Apr 10, 2024 4:00pm
Amylyx stock slips 6% after phase 2 rare disease data drop
Apr 10, 2024 2:48pm
ACC: Efficacy ticks down a smidge for Ionis' metabolic drug
Apr 7, 2024 9:45am
J&J targets rare maternal-fetal disease: 'We're going for this'
Apr 2, 2024 11:23am
Applied Tx’s pediatric rare disease prosect hits another snag
Mar 29, 2024 10:21am