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rare diseases
Biotech
J&J funds Rallybio in risk-busting rare pregnancy disease pact
J&J is partnering with Rallybio in a new pact designed to reduce the risk of a rare maternal-fetal blood disorder.
Gabrielle Masson
Apr 10, 2024 4:00pm
Amylyx stock slips 6% after phase 2 rare disease data drop
Apr 10, 2024 2:48pm
ACC: Efficacy ticks down a smidge for Ionis' metabolic drug
Apr 7, 2024 9:45am
J&J targets rare maternal-fetal disease: 'We're going for this'
Apr 2, 2024 11:23am
Applied Tx’s pediatric rare disease prosect hits another snag
Mar 29, 2024 10:21am
Nanoscope eyes market after phase 2b retinal disease data drop
Mar 26, 2024 7:00am